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Sep 02, 2026 10:14 PM ET
Signal
FDA/Bio
Ultragenyx Announces Phase 3 Aspire results in Angelman Syndrome
Phase 3 Aspire results provide pivotal efficacy data for Angelman Syndrome treatment.
What changed
Why it matters
Phase 3 Aspire results provide pivotal efficacy data for Angelman Syndrome treatment.
Sources
eodhd
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