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Sep 18, 2026 01:51 PM ET
Catalyst
FDA/Bio
Abeona Therapeutics® Congratulates Ultragenyx on U.S. FDA Approval of FAYUVI™ Gene Therapy for Sanfilippo Syndrome Type A (MPS IIIA)
FDA approval of gene therapy for Sanfilippo Syndrome validates sector catalyst.
What changed
FDA approval of gene therapy for Sanfilippo Syndrome validates sector catalyst.
Why it matters
FDA approval of gene therapy for Sanfilippo Syndrome validates sector catalyst. — impact context not separately stored; see What changed.
Sources
eodhd
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